Cure for thalassemia major – from allogeneic hematopoietic stem cell transplantation to gene therapy | Haematologica
PDF) Cure for thalassemia major – From allogeneic hematopoietic stem cell transplantation to gene therapy
Gene therapies for transfusion dependent β‐thalassemia: Current status and critical criteria for success - Soni - 2020 - American Journal of Hematology - Wiley Online Library
Β-Thalassemias | NEJM
Guidelines for the Management of Non-Transfusion Dependent Thalassaemias (2nd edition - 2017) by Thalassaemia International Federation (TIF) - Issuu
Medicina | Free Full-Text | Non-Transfusion-Dependent Thalassemia: A Panoramic Review
JCM | Free Full-Text | Does Hepcidin Tuning Have a Role among Emerging Treatments for Thalassemia?
A systematic review of quality of life in sickle cell disease and thalassemia after stem cell transplant or gene therapy - ScienceDirect
Cure for thalassemia major – from allogeneic hematopoietic stem cell transplantation to gene therapy | Haematologica
Survival and complications in patients with haemoglobin E thalassaemia in Sri Lanka: a prospective, longitudinal cohort study - The Lancet Global Health
Frontiers | The Future of Gene Therapy for Transfusion-Dependent Beta- Thalassemia: The Power of the Lentiviral Vector for Genetically Modified Hematopoietic Stem Cells
IJMS | Free Full-Text | Hepatocellular Carcinoma in β-Thalassemia Patients: Review of the Literature with Molecular Insight into Liver Carcinogenesis
Thalassaemia - The Lancet
Cureus | Blood Demand and Challenges for Patients With Beta-Thalassemia Major in Eastern Saudi Arabia | Article
A paradigm shift on beta-thalassaemia treatment: How will we manage this old disease with new therapies? - ScienceDirect
Novel genetic therapeutic approaches for modulating the severity of β‑ thalassemia (Review)
Full article: Revisiting beta thalassemia intermedia: past, present, and future prospects
Current status of beta‐thalassemia and its treatment strategies - Ali - 2021 - Molecular Genetics & Genomic Medicine - Wiley Online Library
Biomolecules | Free Full-Text | Epigenetic Insights and Potential Modifiers as Therapeutic Targets in β–Thalassemia
Cure for thalassemia major – from allogeneic hematopoietic stem cell transplantation to gene therapy | Haematologica
Cureus | Efficacy and Safety of Luspatercept in the Treatment of β- Thalassemia: A Systematic Review | Article
JCM | Free Full-Text | Does Hepcidin Tuning Have a Role among Emerging Treatments for Thalassemia?
Beta Thalassemia: New Therapeutic Options Beyond Transfusion and Iron Chelation | SpringerLink
Plasma proteome profiling combined with clinical and genetic features reveals the pathophysiological characteristics of β-thalassemia - ScienceDirect
